rickets, osteomalacia and renal osteodystrophy

Rickets and osteomalacia

definition

·      deficiency of calcium and/or phosphorus for mineralisation of the skeleton

·      leads to less mineralised bone per unit volume of bone

·      rickets

·      increased uncalcified osteoid in the immature skeleton (children)

·      osteomalacia

·      increased uncalcified osteoid in the mature skeleton (adults)

aetiology

·      vitamin D deficiency is classic form of disease

·      now much less common

·      most common cause now is hypophosphataemic rickets

Causes

·      deficiency states

·      vitamin D

·      calcium

·      phosphate

·      gastrointestinal

·      vitamin D resistance

·      phosphaturic

·      type-1 dependent

·      type-II dependent

·      renal tubular acidosis

·      renal osteodystrophy

pathophysiology
Deficiency states

General

Calcium and vitamin D

·      reduced vitamin D intake leads to

·      decrease in calcium absorption from gut leads to

·      decreased serum Ca++ leads to

·      secondary hyperparathyroidism leads to

·      increase of serum Ca++ to low normal and

·      phosphate diuresis with decrease of serum phosphate

Calcium

·      decrease in calcium intake leads to

·      decreased serum Ca++ leads to

·      secondary hyperparathyroidism leads to

·      increase of serum Ca++ to low normal and

·      phosphate diuresis with decrease of serum phosphate

Phosphate

·      decrease in phosphate intake leads to

·      decreased serum PO4-- leads to

·      increased renal production of 1,25-vit D leads to

·      increased bone resorption

Vitamin D deficiency

·      classic form

·      usually results from

·      dietary deficiency of vitamin D (elderly, vegans)

·      inadequate exposure to sunlight

·      overcome by vitamin D and calcium supplements

Calcium deficiency

·      decreased dietary intake

·      seen where dairy products avoided

Chelators

·      very uncommon

·      seen with bizarre diet

·      substances that can bind calcium and make it unabsorbable are

·      phytate (cereals)

·      oxalate (spinach)

·      phosphate excess

Phosphorus deficiency

·      dietary cause very unusual

·      may be due to precipitation of insoluble phosphates by

·      beryllium (industrial toxin)

·      aluminium (in antacids)

Gastrointestinal causes

Gastric

·      seen previously with surgery for peptic ulcer disease

·      result of Polya or Billroth II gastrectomy

·      decreased absorption of calcium due to

·      decreased acid content in stomach

·      excessively rapid transit of contents through duodenum and proximal jejunum (‘dumping’)

Biliary

·      reduced vitamin D absorption due to abnormal fat metabolism

·      associated with

·      failure of emulsifying action of bile salts

·      presence of free fat in GIT

·      may be reduced calcium absorption

·      from production of insoluble calcium soaps with free fatty acids

Enteric

·      decreased calcium absorption from diffuse injury to wall of small bowel

·      inflammatory bowel disease

·      shunts or fistulae

·      rapid transit

Renal tubular causes

Hypophosphataemic

·      most prevalent cause of rickets

·      due to genetic or aquired defect in handling of phosphate in proximal tubule

·      no secondary hyperparathyroidism because serum calcium not affected

·      thus no excessive resorption

·      administration of vitamin D has little effect

·      overcome by administration of phosphate

·      congenital and acquired forms

X-linked hypophosphataemia

·      Albright’s syndrome

·      most common congenital form

·      X-linked dominant disorder

·      diminished tubular reabsorption of phosphate

·      treated with administration of high doses of phosphate

·      high doses of vitamin D added to offset secondary hyperparathyroidism

Vitamin D dependent

·      rare disorders

·      classical features of vitamin D deficiencies

·      psuedodependence as no response to vitamin D replacement

·      overcome by administration of high doses of 1,25-D and calcium

Type I

·      failure of conversion of 25-D to 1,25-D

·      may be due to abnormality of renal alpha-hydroxylase

Type II

·      end-organ insensitivity to 1,25-D

·      may be due to failure of gut and other cells to recognise 1,25-D

Renal tubular acidosis

·      may be

·      primary genetic syndrome

·      acquired syndrome

·      part of another disorder

·      part of another renal tubular syndrome

·      caused by inability for kidney to conserve bicarbonate

·      leads to decreased serum bicarbonate and acidosis

·      result is

·      erosion of bone from metabolic acidosis

·      release of calcium from bone as carbonate used as buffer

·      calcium excretion in urine

·      cannot be treated by vitamin D

·      overcome by correction of metabolic acidosis with sodium bicarbonate

Fanconi’s syndrome

·      generalised defect in renal proximal tubular transport

·      impaired resorption of paphate, glucose, amino acids etc

·      excessive excretion of calcium

·      heterogenous group of causes

·      due to

·      inherited disorders

·      metabolic or toxic injury to proximal tubule

·      rickets and osteomalacia from

·      phosphaturia

·      hypercalcuria

·      abnormal vitamin D metabolism

Unusual causes

Hypophosphatasia

·      rare inherited form

·      due to generalised reduction in tissue non-specific alkaline phosphatase activity

·      causes retardation of skeletal mineralisation

·      often severe and fatal

Fibrous dysplasia or neurofibromatosis

·      rickets or osteomalacia may be rare manifestations

Bone and soft tissue tumours

·      most common in benign fibrous soft-tissue tumours

·      due to production of humoral factors that affect renal tubule

·      esp. phosphate handling

Chronic use of anticonvulsants

·      with all anti-seizure drugs

·      due to interference with hepatic handling of vitamin D

·      vit D converted to inactive metabolites rather than 25-D

pathology
Histology

·      cortices thin

·      trabeculae thin and irregular

·      osteoid seams

·      layer of unmineralized bone

·      surrounds a mineralized segment

Physis in rickets

·      reserve and proliferative zones are essentially normal

·      hypertrophic zone disordered

·      greatly widened and increased in height

·      orderly columnization lost

·      tongues of hypertrophic cells extend down into metaphysis

·      height increased because cells do not release calcium and remain alive

·      metaphysis abnormal

·      matrix does not calcify

·      few spicules of bone that do form are poorly mineralized

·      wide osteoid seams present

clinical
Rickets

Growth

·      stunting of height

·      weight not affected

·      may have enlarged abdomen (rachitic pot-belly)

Activity

·      apathy and hypokinesis

·      irritability

·      weakness

·      may be severe with inability to walk

Skull

·      softening (craniotabes)

·      prominence of sutures (hot-cross skull)

·      prominence of frontal bones (frontal bossing)

Teeth

·      defects of enamel

·      extensive caries

Thorax

·      prominence of costochondral junctions (rachitic rosary)

·      pectus carinatum

·      indenation of lower part of rib cage at insertion of diaphragm (Harrison’s groove)

Spine

·      thoracic kyphosis (rachitic cat-back)

Extremities

·      enlagement of wrists, elbows, ankles and knees

·      bowing deformity of long bones

·      esp. lower extremity - bow legs and knock knees

·      pathological fractures

Osteomalacia

·      few findings

·      malaise and easy fatiguability

·      bone pain and tenderness

·      may present with back pain

·      proximal muscle weakness

·      Trendelenburg gait

investigations
Biochemical

·      low or low-normal Ca++

·      low PO4-

·      calcium/phosphate index low

·      Ca++ x PO4- < 2.4 (normal > 3)

·      high ALP

·      PTH normal or high

·      low serum 25-D

Plain radiology

General

·      rickets

·      primarily affects growth plate but also bones

·      bones may show changes of secondary hyperparathyroidism

·      osteomalacia

·      affects only bones

·      changes less evident because bones less active

·      may also see changes of secondary hyperparathyroidism

·      osseous changes

·      thin cortices

·      indistinct fuzzy trabeculae with ground-glass appearance

·      may be

·      bowing

·      pathological fractures

Rickets

·      growth plate changes characteristic

Physis

·      enormous increase in height of growth plate

·      irregular cupping and flaring of metaphysis

·      failure of mineralisation of metaphysis

Secondary hyperparathyroidism

·      subperiosteal erosions

·      in areas of maximal remodelling

·      medial borders of

·      proximal humerus

·      femoral neck

·      distal femur

·      proximal tibia

·      lateral borders of

·      distal radius

·      distal ulna

Osteomalacia

·      three characteristic features

Looser's zones

·      syn. Milkman's pseudofractures

·      ribbon-like linear radiolucent lines

·      transverse to long axis of bone

·      often do not extend completely across bone

·      are stress fractures that have healed with unmineralised callus

·      occur on concave side of long bones

·      medial femoral neck

·      ischial and pubic rami

·      ribs, clavicles

·      axillary border of scapulae

·      may propagate

Codfish vertebrae

·      may be multiple vertebral compression fractures from disc pressure

·      result is biconcave (codfish) vertebrae

Trefoil pelvis

·      billateral indentation of acebulum

·      gives appearance of champagne glass or trefoil

Bone scan

·      patchy areas of increased uptake

·      Looser’s zones are active

Renal Osteodystrophy

·      much less common because of improved management of patients with renal failure

definition

·      rickets or osteomalacia plus secondary hyperparathyroidism as a result of glomerular failure

pathophysiology

·      glomerular failure leads to

·      failure of filtration and retention of phosphate leads to

·      hyperphosphataemia and

·      decreased tubular mass leads to

·      decreased synthesis of 1,25-D and

·      increased phosphate level in GIT cells leads to

·      decreased calcium absorption leads to

·      decreased serum Ca++ leads to

·      secondary hyperparathyroidism leads to

·      defect in bone mineralisation leads to

·      low-normal serum Ca++ leads to

·      ectopic calcification and ossification and osteosclerosis

Aluminium toxicity

·      in patients on prolonged haemodialysis, condition may not respond to 1,25-D

·      may be due to aluminium intoxication

·      aluminium-containing phosphate-binding antacids used in haemodialysis fluid to control phosphate accumulation

clinical

·      features of rickets or osteomalacia

·      features of hyperparathyroidism

·      slipped upper femoral epiphysis

·      patchy osteosclerosis

·      vertebral sclerosis may be in upper and lower thirds of bodies (rugger jersey spine)

·      ectopic calcification and ossification

·      conjunctivae (red eyes)

·      blood vessels (media and muscularis)

·      skin (itching)

·      periarticular (frozen joints)

Management

Prevention

·      adoption of appropriate diets

·      dietary supplements

·      sun exposure

Treatment

General

·      agents

·      vitamin D

·      1,25-D

·      alpha-hydroxylase

·      calcium

·      phosphate

·      dialysis

·      subtotal parathyroidectomy

Orthopaedic

·      establish diagnosis

·      fixation of fractures

·      bracing or osteotomy of deformity

·      fixation of slipped epiphysis

·      realignment or replacement of damaged joints